‘Promising Pathway Act’ Will Save Lives Over and Above ‘Right to Try’ and ‘Expanded Access’

The best hope for these Americans and future generations facing terminal and rare diseases is the recently reintroduced Promising Pathway Act.
‘Promising Pathway Act’ Will Save Lives Over and Above ‘Right to Try’ and ‘Expanded Access’
The U.S. Food and Drug Administration (FDA) in White Oak, Md., on June 5, 2023. Madalina Vasiliu/The Epoch Times
Siri Terjesen
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Commentary
Approximately one in every ten Americans is affected by one of approximately 7,000 rare diseases, of which many are terminal. For many of these diseases, fully Food and Drug Administration (FDA)-approved cures are not yet available, and in some cases, cures may be available, but take too long to reach the patients. For example, approximately 300 children in America are diagnosed with DIPG (diffuse intrinsic pontine glioma), a rare and highly aggressive brain cancer with a life expectancy of under one year.
Siri Terjesen
Siri Terjesen
Author
Dr. Siri A. Terjesen is associate dean, research & external relations, founding executive director of the Madden Center for Value Creation.
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